Fonte dati per questo evento: Agenas. Evento organizzato da provider terzo. Trova ECM riporta dati pubblici dell'evento a scopo informativo e non è responsabile né del corso né dei contenuti, né ha accordi commerciali o di collaborazione con il provider.
Questo corso ECM di tipo FAD Sincrona è offerto da Biba Tour Srl e assegna 6 crediti ECM. L'obiettivo formativo è: 2 - Linee guida - protocolli - procedure.
FAD sincrona internazionale su terapia dell'emofilia: factor replacement (efanesoctocog alfa), strategie di rebalancing, gene therapy e gene editing. Relatori italiani e internazionali. 6 crediti ECM, 13 novembre 2026.
The therapeutic landscape of hemophilia is undergoing a profound transformation. While the field is rapidly expanding beyond conventional replacement therapy toward rebalancing strategies, gene therapy, and gene editing, replacement treatment itself is also entering a new phase of innovation.
In particular, the availability of novel factor replacement approaches, including high-sustained factor VIII therapies such as efanesoctocog alfa, is reshaping expectations in prophylaxis, bleed protection, treatment personalization, and quality of life. These advances are broadening the clinical possibilities within replacement therapy and are redefining how clinicians position factor-based strategies in relation to non-replacement options.
At the same time, the emergence of rebalancing therapies, RNA interference approaches, AAV-based gene therapy, and gene editing is creating an increasingly complex decision-making environment for hemophilia treatment centers. Key issues now include treatment selection, patient profiling, monitoring, long-term safety, durability of response, access, sustainability, and future care pathways.
Webinar Garden 2026 aims to provide a multidisciplinary update on the most recent advances, integrating clinical evidence, real-world data, international consensus recommendations, and the patient perspective, with the goal of outlining the future management of coagulation disorders in the era of advanced therapies.
13/11/2026 · Online (piattaforma FAD sincrona – Webinar), Via Emilia 38, Palermo
Iscrizione online: http://www.bibagroup.it/eventi-biba/ (piattaforma FAD sincrona, provider BIBA Tour srl, ID 1420).
Fonte dati per questo evento: Agenas. Evento organizzato da provider terzo. Trova ECM riporta dati pubblici dell'evento a scopo informativo e non è responsabile né del corso né dei contenuti, né ha accordi commerciali o di collaborazione con il provider.